The Kang Laboratory at Vanderbilt University identified that the drug 4-phenylbutyrate can restore GABA uptake for SLC6A1 patients leading to a 70% seizure reduction rate.
SLC6A1 Connect and STXBP1 Foundation are currently sponsoring a drug repurposing trial with a renewed sense of hope and optimism for our children. You are our hero, Dr. Kang!!!!